Drug Development for Rare Diseases by Bo Yang (University of Arizona, Tucson, Arizona, USA)
* Innovative clinical trial design
* Regulatory approval
* Real world evidence
Drug Development for Rare Diseases
Drug Development for Rare Diseases
$139.34
Condition - Very Good
Only 1 left
Summary
A disease is defined as rare if the prevalence is fewer than 200,000 in the United States. It is estimated that there are more than 7,000 rare diseases, which collectively affect 30 million Americans. This diverse and complex disease area poses challenges for patients, caregivers, regulators, drug developers and other stakeholders.
Faster Shipping
Get this product faster from our US warehouse
Drug Development for Rare Diseases Summary
About Bo Yang (University of Arizona, Tucson, Arizona, USA)
Bo Yang is the Vice President, Biometrics and Real World Evidence at Vertex Pharmaceuticals, USA.
Yang Song is the Executive Director, Biostatistics Group Head of Pipeline Development at Vertex Pharmaceuticals, USA.
Yijie Zhou is the Executive Director, Real World Statistics and Analytics at Vertex Pharmaceuticals, USA.
Table of Contents
1. Introduction to Rare Disease Therapy Development 2. Challenges and Opportunities in Rare Disease Drug 3. Developing Drugs for Rare Diseases: Regulatory Strategies 4. Clinical Trial Design and Analysis Considerations for Rare Diseases 5. Use of Real-World Evidence to Support Drug Development 6. Clinical Development of Pediatric Program within Rare Diseases 7. Use of Modeling and Simulation in Support of Drug Development for Rare Diseases 8. Case Studies of Rare Disease Drug Development
Additional information
CIN0367518341VG
9780367518349
0367518341
Drug Development for Rare Diseases by Bo Yang (University of Arizona, Tucson, Arizona, USA)
Used - Very Good
Hardback
Taylor & Francis Ltd
2023-02-13
222
N/A
Book picture is for illustrative purposes only, actual binding, cover or edition may vary.
This is a used book - there is no escaping the fact it has been read by someone else and it will show signs of wear and previous use. Overall we expect it to be in very good condition, but if you are not entirely satisfied please get in touch with us